Nonviral base editing of KCNJ13 mutation preserves vision in a model of inherited retinal channelopathy.

At 10 weeks after injection, the c wave was reduced (0.7 ± 0.1) for the nontargeted retina compared with an increasing trend (1.6 ± 0.1, P = 0.01) ( Figure 6K ) for the targeted guide–delivered retina.

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