<i>In vivo</i> adenine base editing rescues brain biochemistry and improves motor deficits in a common phenylketonuria variant.

Linear regression modeling produced an R 2 value of 0.92, indicating a highly significant relationship between hepatic editing and reduced plasma Phe levels post-treatment (F(1,6) = 71.31, p < 0.001) ( Figure 1 C).

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