Perspectives on Gene Therapy: Choroideremia Represents a Challenging Model for the Treatment of Other Inherited Retinal Degenerations.

The modest, borderline significant improvement in VA in a minority of patients in this study echoes previous reports from the ongoing CHM gene therapy trials. 43 – 46 , 62 – 64 Less than 20% of the treated patients, reported thus far, have achieved only modest improvements in acuity in their treated eyes; this emphasizes that, when

also in 11,409 other papers