nominally significantP = 0.0050
In the Results, in the “Part B cohort with infantile-onset SMA: neurodegeneration” section, the text “...compared with the ENDEAR matched sham group (30% reduction)” has been corrected to “...compared with the ENDEAR matched sham group (32% reduction)”, and “nominally significant P = 0.0050” has been corrected to “nominally significant P = 0.0075”.