Downstream Pathways of Dystrophin Deficiency in Duchenne Muscular Dystrophy: Implications for Muscle Degeneration and Regeneration.

Similarly, Edasalonexent, a dual NF‐κB inhibitor, was well tolerated and showed a trend toward slowing disease progression in younger paediatric DMD patients, although it did not meet its primary efficacy endpoints and further development was discontinued [ 115 ].

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