Significant improvements in 12-minute-walk test, nearly significant improvement in 3-minute stair climb and significant reduction in uGAG levels were demonstrated in the 24-week, randomized, double-blind Phase 3 trial [ 102 ].
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Significant improvements in 12-minute-walk test, nearly significant improvement in 3-minute stair climb and significant reduction in uGAG levels were demonstrated in the 24-week, randomized, double-blind Phase 3 trial [ 102 ].