Development, clinical utility, and place of ivacaftor in the treatment of cystic fibrosis.

However, a larger randomized, multicenter, double-blind, placebo-controlled trial which followed 174 boys with Duchenne muscular dystrophy showed the primary endpoint of the six-minute walk test did not reach statistical significance. 58 Other potential treatments in clinical trials The knowledge base surrounding the structure and function of CFTR that has accumulated in the last 20 years continues to grow.

also in 111,027 other papers